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Titolo Data di pubblicazione Autori Rivista Serie Titolo libro
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3 2022 Martina ScanoAlberto BenetolloLeonardo NogaraMichela BondìFrancesco Dalla BarbaMichela SoardiAkyurek Eylem EmekPaola CaccinMarcello CarottiRoberta SacchettoBert BlaauwDorianna Sandonà + HUMAN MOLECULAR GENETICS - -
Zebrafish as a model for sarcoglycanopathies: in-depth analysis of the disease phenotype 2022 Francesco Dalla BarbaMichela SoardiMartina ScanoAlberto BenetolloMarcello CarottiPaola CaccinGiovanni RisatoFrancesco ArgentonDorianna Sandonà - - ZFIM 2022 3RD ITALIAN ZEBRAFISH MEETING
In vivo rescue of α-sarcoglycan mutants by CFTR correctors 2021 Martina ScanoAlberto BenetolloMichela BondìPaola CaccinMarcello CarottiFrancesco Dalla BarbaMichela SoardiRoberta SacchettoDorianna Sandonà - - The virtual world conference on rare diseases
In vivo recovery of α-sarcoglycan mutants by protein folding correctors 2021 Martina ScanoAlberto BenetolloMichela BondìPaola CaccinMarcello CarottiFrancesco Dalla BarbaMichela SoardiRoberta SacchettoDorianna Sandonà EUROPEAN JOURNAL OF TRANSLATIONAL MYOLOGY - -
In vivo recovery of α-sarcoglycan mutants by protein folding correctors 2021 Martina ScanoAlberto BenetolloMichela BondìPaola CaccinMarcello CarottiFrancesco Dalla BarbaMichela SoardiRoberta SacchettoDorianna Sandonà - - 2021 Padua Days on Myology & Mobility Medicine
Combined Use of CFTR Correctors in LGMD2D Myotubes Improves Sarcoglycan Complex Recovery 2020 Marcello CarottiMartina ScanoIrene FancelloGiovanni RisatoMichela SoardiDorianna Sandonà + INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES - -
Novel zebrafish models for sarcoglycanopathy 2019 Michela SoardiMarcello CarottiGiovanni RisatoMartina ScanoFrancesco ArgentonRoberta SacchettoDorianna Sandonà + EUROPEAN JOURNAL OF TRANSLATIONAL MYOLOGY - -
Small molecules to rescue folding-defective sarcoglycans: in vivo assessment of novel therapeutic strategies 2019 Dorianna SandonaMartina ScanoChiara FecchioMichela BondiMarcello CarottiGiovanni RisatoMichela SoardiRoberta Sacchetto - - XX Scientific Convention Telethon
Novel animal models for sarcoglycanopathy 2019 Martina ScanoGiovanni RisatoMichela SoardiMarcello CarottiDorianna Sandonà EUROPEAN JOURNAL OF TRANSLATIONAL MYOLOGY - -
Generation of novel zebrafish models of sarcoglycanopathy 2018 Soardi, Michela - - -
Repairing folding-defective α-sarcoglycan mutants by CFTR correctors, a potential therapy for Limb Girdle Muscular Dystrophy 2D 2018 Carotti, MarcelloSOARDI, MICHELABianchini, ElisaGomiero, ChiaraFecchio, ChiaraSacchetto, RobertaSandonà, Dorianna + HUMAN MOLECULAR GENETICS - -
Sarcoglycanopathies, therapeutic approaches based on small molecules 2018 Dorianna SandonàChiara FecchioMarcello CarottiMichela SoardiElisa BianchiniRoberta Sacchetto - - 13th Meeting of the Mediterranean Society of Myology in connection with the 2nd Congress of the Turkish Neuromuscular Society
From the molecular mechanism to novel pharmacological approaches, the story of a muscular dystrophy. 2017 Dorianna Sandona’Marcello CarottiChiara FecchioMichela Soardi - - INTERNATIONAL SYMPOSIUM-CUM-TRAINING COURSE ON MOLECULAR MEDICINE AND DRUG RESEARCH (MMDR-6)
Mostrati risultati da 1 a 13 di 13
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