BIFFI, ALESSANDRA
BIFFI, ALESSANDRA
Dipartimento di Salute della Donna e del Bambino - SDB
Restoration of bacterial killing activity of human respiratory cystic fibrosis cells through cationic vector-mediated cystic fibrosis transmembrane conductance regulator gene transfer
1999 Biffi, Alessandra; Sersale, Giovanna; Cassetti, Arianna; Villa, Antonello; Bordignon, Claudio; Assael, Baroukh M.; Conese, Massimo
Comparison between cationic polymers and lipids in mediating systemic gene delivery to the lungs
1999 Bragonzi, A.; Boletta, A.; Biffi, A.; Muggia, A.; Sersale, G.; Cheng, S. H.; Bordignon, C.; Assael, B. M.; Conese, M.
Biodistribution and transgene expression with nonviral cationic vector/DNA complexes in the lungs
2000 Bragonzi, A.; Dina, G.; Villa, A.; Calori, G.; Biffi, A.; Bordignon, C.; Assael, B. M.; Conese, M.
Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells
2004 Biffi, A.; De Palma, M.; Quattrini, A.; Del Carro, U.; Amadio, S.; Visigalli, I.; Sessa, M.; Fasano, S.; Brambilla, R.; Marchesini, S.; Bordignon, C.; Naldini, L.
Gene therapy of storage disorders by retroviral and lentiviral vectors
2005 Biffi, A.; Naldini, L.
Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters
2005 Amendola, M.; Venneri, M. A.; Biffi, A.; Vigna, E.; Naldini, L.
Somatic intragenic recombination of the arylsulfatase A gene in a metachromatic leukodystrophy patient
2006 Regis, S.; Lualdi, S.; Biffi, A.; Sessa, M.; Corsolini, F.; Parenti, G.; Filocamo, M.
Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice
2006 Biffi, A.; Capotondo, A.; Fasano, S.; Del Carro, U.; Marchesini, S.; Azuma, H.; Malaguti, M. C.; Amadio, S.; Brambilla, R.; Grompe, M.; Bordignon, C.; Quattrini, A.; Naldini, L.
SUMF1 enhances sulfatase activities in vivo in five sulfatase deficiencies
2007 Fraldi, A.; Biffi, A.; Lombardi, A.; Visigalli, I.; Pepe, S.; Settembre, C.; Nusco, E.; Auricchio, A.; Naldini, L.; Ballabio, A.; Cosma, M. P.
Novel candidate disease for gene therapy: Metachromatic leukodystrophy
2007 Biffi, A.; Naldini, L.
Safety of arylsulfatase A overexpression for gene therapy of metachromatic leukodystrophy
2007 Capotondo, A.; Cesani, M.; Pepe, S.; Fasano, S.; Gregori, S.; Tononi, L.; Venneri, M. A.; Brambilla, R.; Quattrini, A.; Ballabio, A.; Cosma, M. P.; Naldini, L.; Biffi, A.
Gene therapy of lysosomal storage disorders by lentiviral vectors
2007 Biffi, A.; Naldini, L.
Metachromatic leukodystrophy: An overview of current and prospective treatments
2008 Biffi, A.; Lucchini, G.; Rovelli, A.; Sessa, M.
Human hematopoietic stem cells in gene therapy: Pre-clinical and clinical issues
2008 Biffi, A.; Cesani, M.
Metachromatic leukodystrophy - Mutation analysis provides further evidence of genotype-phenotype correlation
2008 Biffi, A.; Cesani, M.; Fumagalli, F.; Del Carro, U.; Baldoli, C.; Canale, S.; Gerevini, S.; Amadio, S.; Falautano, M.; Rovelli, A.; Comi, G.; Roncarolo, M. G.; Sessa, M.
Dlg1, Sec8, and Mtmr2 regulate membrane homeostasis in Schwann cell myelination
2009 Bolis, A.; Coviello, S.; Visigalli, I.; Taveggia, C.; Bachi, A.; Chishti, A. H.; Hanada, T.; Quattrini, A.; Previtali, S. C.; Biffi, A.; Bolino, A.
Monitoring disease evolution and treatment response in lysosomal disorders by the peripheral benzodiazepine receptor ligand PK11195
2009 Visigalli, I.; Moresco, R. M.; Belloli, S.; Politi, L. S.; Gritti, A.; Ungaro, D.; Matarrese, M.; Turolla, E.; Falini, A.; Scotti, G.; Naldini, L.; Fazio, F.; Biffi, A.
Specific determination of β-galactocerebrosidase activity via competitive inhibition of β-galactosidase
2009 Martino, S.; Tiribuzi, R.; Tortori, A.; Conti, D.; Visigalli, I.; Lattanzi, A.; Biffi, A.; Gritti, A.; Orlacchio, A.
Development and maturation of invariant NKT cells in the presence of lysosomal engulfment
2009 Plati, T.; Visigalli, I.; Capotondo, A.; Buono, M.; Naldini, L.; Cosma, M. P.; Biffi, A.
Characterization of new arylsulfatase a gene mutations reinforces genotype-phenotype correlation in metachromatic leukodystrophy
2009 Cesani, M.; Capotondo, A.; Plati, T.; Sergi, L. S.; Fumagalli, F.; Roncarolo, M. G.; Naldini, L.; Comi, G.; Sessa, M.; Biffi, A.