BIFFI, ALESSANDRA

BIFFI, ALESSANDRA  

Dipartimento di Salute della Donna e del Bambino - SDB  

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Risultati 1 - 20 di 137 (tempo di esecuzione: 0.029 secondi).
Titolo Data di pubblicazione Autori Rivista Serie Titolo libro
Restoration of bacterial killing activity of human respiratory cystic fibrosis cells through cationic vector-mediated cystic fibrosis transmembrane conductance regulator gene transfer 1999 Biffi, Alessandra + HUMAN GENE THERAPY - -
Comparison between cationic polymers and lipids in mediating systemic gene delivery to the lungs 1999 Biffi, A. + GENE THERAPY - -
Biodistribution and transgene expression with nonviral cationic vector/DNA complexes in the lungs 2000 Biffi, A. + GENE THERAPY - -
Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells 2004 Biffi A. + THE JOURNAL OF CLINICAL INVESTIGATION - -
Gene therapy of storage disorders by retroviral and lentiviral vectors 2005 Biffi A. + HUMAN GENE THERAPY - -
Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters 2005 Biffi A. + NATURE BIOTECHNOLOGY - -
Somatic intragenic recombination of the arylsulfatase A gene in a metachromatic leukodystrophy patient 2006 Biffi A. + MOLECULAR GENETICS AND METABOLISM - -
Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice 2006 Biffi A. + THE JOURNAL OF CLINICAL INVESTIGATION - -
SUMF1 enhances sulfatase activities in vivo in five sulfatase deficiencies 2007 Biffi A. + BIOCHEMICAL JOURNAL - -
Novel candidate disease for gene therapy: Metachromatic leukodystrophy 2007 Biffi A. + EXPERT OPINION ON BIOLOGICAL THERAPY - -
Safety of arylsulfatase A overexpression for gene therapy of metachromatic leukodystrophy 2007 Biffi A. + HUMAN GENE THERAPY - -
Gene therapy of lysosomal storage disorders by lentiviral vectors 2007 Biffi A. + - - Lysosomal Storage Disorders
Metachromatic leukodystrophy: An overview of current and prospective treatments 2008 Biffi A. + BONE MARROW TRANSPLANTATION - -
Human hematopoietic stem cells in gene therapy: Pre-clinical and clinical issues 2008 Biffi A. + CURRENT GENE THERAPY - -
Metachromatic leukodystrophy - Mutation analysis provides further evidence of genotype-phenotype correlation 2008 Biffi A.Sessa M. + CLINICAL GENETICS - -
Dlg1, Sec8, and Mtmr2 regulate membrane homeostasis in Schwann cell myelination 2009 Biffi A. + THE JOURNAL OF NEUROSCIENCE - -
Monitoring disease evolution and treatment response in lysosomal disorders by the peripheral benzodiazepine receptor ligand PK11195 2009 Biffi A. + NEUROBIOLOGY OF DISEASE - -
Specific determination of β-galactocerebrosidase activity via competitive inhibition of β-galactosidase 2009 Biffi A. + CLINICAL CHEMISTRY - -
Development and maturation of invariant NKT cells in the presence of lysosomal engulfment 2009 Biffi A. + EUROPEAN JOURNAL OF IMMUNOLOGY - -
Characterization of new arylsulfatase a gene mutations reinforces genotype-phenotype correlation in metachromatic leukodystrophy 2009 Biffi A. + HUMAN MUTATION - -