DALLA BARBA, FRANCESCO
DALLA BARBA, FRANCESCO
Università di Padova
C17 corrector for the treatment of sarcoglycanopathy: preliminary ADME studies
2022 Benetollo, Alberto; Scano, Martina; Parrasia, Sofia; Biasutto, Lucia; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sandona', Dorianna
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3
2021 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondi', Michela; DALLA BARBA, Francesco; Soardi, Michela; Sandra, Furlan; Akyurek, EYLEM EMEK; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandona', Dorianna
In vivo proof of concept of the efficacy of the CFTR corrector C17 in a sarcoglycanopathy mouse model
2021 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondi', Michela; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo rescue of α-sarcoglycan mutants by CFTR correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
Zebrafish as a model for sarcoglycanopathies: in-depth analysis of the disease phenotype
2022 DALLA BARBA, Francesco; Soardi, Michela; Scano, Martina; Benetollo, Alberto; Carotti, Marcello; Caccin, Paola; Risato, Giovanni; Argenton, Francesco; Sandona', Dorianna