SCANO, MARTINA
SCANO, MARTINA
Dipartimento di Scienze Biomediche - DSB
Advanced therapeutic approaches in sarcoglycanopathies
2024 Scano, M.; Benetollo, A.; Dalla Barba, F.; Sandona, D.
C17 corrector for the treatment of sarcoglycanopathy: preliminary ADME studies
2022 Benetollo, Alberto; Scano, Martina; Parrasia, Sofia; Biasutto, Lucia; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sandona', Dorianna
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3
2022 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondì, Michela; DALLA BARBA, Francesco; Soardi, Michela; Furlan, Sandra; Akyurek, EYLEM EMEK; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandonà, Dorianna
Combined Use of CFTR Correctors in LGMD2D Myotubes Improves Sarcoglycan Complex Recovery
2020 Carotti, Marcello; Scano, Martina; Fancello, Irene; Richard, Isabelle; Risato, Giovanni; Bensalah, Mona; Soardi, Michela; Sandonà, Dorianna
Efficacy of Cystic Fibrosis Transmembrane Regulator Corrector C17 in Beta-Sarcoglycanopathy—Assessment of Patient’s Primary Myotubes
2024 Scano, Martina; Benetollo, Alberto; Dalla Barba, Francesco; Akyurek, Eylem Emek; Carotti, Marcello; Sacchetto, Roberta; Sandonà, Dorianna
I correttori del CFTR come nuovo approccio farmacologico per le sarcoglicanopatie
2021 Scano, Martina
In vivo proof of concept of the efficacy of the CFTR corrector C17 in a sarcoglycanopathy mouse model
2021 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondi', Michela; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo rescue of α-sarcoglycan mutants by CFTR correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
Modeling Sarcoglycanopathy in Danio rerio
2023 Dalla Barba, Francesco; Soardi, Michela; Mouhib, Leila; Risato, Giovanni; Akyürek, Eylem Emek; Lucon-Xiccato, Tyrone; Scano, Martina; Benetollo, Alberto; Sacchetto, Roberta; Richard, Isabelle; Argenton, Francesco; Bertolucci, Cristiano; Carotti, Marcello; Sandonà, Dorianna
Novel animal models for sarcoglycanopathy
2019 Scano, Martina; Risato, Giovanni; Soardi, Michela; Carotti, Marcello; Sandona', Dorianna
Novel zebrafish models for sarcoglycanopathy
2019 Soardi, Michela; Carotti, Marcello; Bertolucci, Cristiano; Risato, Giovanni; Scano, Martina; Argenton, Francesco; Sacchetto, Roberta; Sandona', Dorianna
Reciprocal homer1a and homer2 isoform expression is a key mechanism for muscle soleus atrophy in spaceflown mice
2022 Blottner, D.; Trautmann, G.; Furlan, S.; Gambara, G.; Block, K.; Gutsmann, M.; Sun, L. -W.; Worley, P. F.; Gorza, L.; Scano, M.; Lorenzon, P.; Vida, I.; Volpe, P.; Salanova, M.
Small molecules to rescue folding-defective sarcoglycans: in vivo assessment of novel therapeutic strategies
2019 Sandona', Dorianna; Scano, Martina; Fecchio, Chiara; Bondi', Michela; Carotti, Marcello; Risato, Giovanni; Soardi, Michela; Sacchetto, Roberta
Synthesis and Evaluation of Bithiazole Derivatives As Potential α-Sarcoglycan Correctors
2023 Ribaudo, Giovanni; Carotti, Marcello; Ongaro, Alberto; Oselladore, Erika; Scano, Martina; Zagotto, Giuseppe; Sandonà, Dorianna; Gianoncelli, Alessandra
The novel use of the CFTR corrector C17 in muscular dystrophy: pharmacological profile and in vivo efficacy
2025 Benetollo, Alberto; Parrasia, Sofia; Scano, Martina; Biasutto, Lucia; Rossa, Andrea; Nogara, Leonardo; Blaauw, Bert; Dalla Barba, Francesco; Caccin, Paola; Carotti, Marcello; Parolin, Alessandro; Akyürek, Eylem Emek; Sacchetto, Roberta; Sandonà, Dorianna
Zebrafish as a model for sarcoglycanopathies: in-depth analysis of the disease phenotype
2022 DALLA BARBA, Francesco; Soardi, Michela; Scano, Martina; Benetollo, Alberto; Carotti, Marcello; Caccin, Paola; Risato, Giovanni; Argenton, Francesco; Sandonà, Dorianna