SOARDI, MICHELA
SOARDI, MICHELA
Dipartimento di Scienze Biomediche - DSB
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3
2022 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondì, Michela; DALLA BARBA, Francesco; Soardi, Michela; Furlan, Sandra; Akyurek, EYLEM EMEK; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandonà, Dorianna
Combined Use of CFTR Correctors in LGMD2D Myotubes Improves Sarcoglycan Complex Recovery
2020 Carotti, Marcello; Scano, Martina; Fancello, Irene; Richard, Isabelle; Risato, Giovanni; Bensalah, Mona; Soardi, Michela; Sandonà, Dorianna
From the molecular mechanism to novel pharmacological approaches, the story of a muscular dystrophy.
2017 Sandona', Dorianna; Carotti, Marcello; Fecchio, Chiara; Soardi, Michela
Generation of novel zebrafish models of sarcoglycanopathy
2018 Soardi, Michela
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo rescue of α-sarcoglycan mutants by CFTR correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
Novel animal models for sarcoglycanopathy
2019 Scano, Martina; Risato, Giovanni; Soardi, Michela; Carotti, Marcello; Sandona', Dorianna
Novel zebrafish models for sarcoglycanopathy
2019 Soardi, Michela; Carotti, Marcello; Bertolucci, Cristiano; Risato, Giovanni; Scano, Martina; Argenton, Francesco; Sacchetto, Roberta; Sandona', Dorianna
Repairing folding-defective α-sarcoglycan mutants by CFTR correctors, a potential therapy for Limb Girdle Muscular Dystrophy 2D
2018 Carotti, Marcello; Marsolier, Justine; Soardi, Michela; Bianchini, Elisa; Gomiero, Chiara; Fecchio, Chiara; Henriques, Sara F; Betto, Romeo; Sacchetto, Roberta; Richard, Isabelle; Sandonà, Dorianna
Sarcoglycanopathies, therapeutic approaches based on small molecules
2018 Sandona', Dorianna; Fecchio, Chiara; Carotti, Marcello; Soardi, Michela; Bianchini, Elisa; Sacchetto, Roberta
Small molecules to rescue folding-defective sarcoglycans: in vivo assessment of novel therapeutic strategies
2019 Sandona', Dorianna; Scano, Martina; Fecchio, Chiara; Bondi', Michela; Carotti, Marcello; Risato, Giovanni; Soardi, Michela; Sacchetto, Roberta
Zebrafish as a model for sarcoglycanopathies: in-depth analysis of the disease phenotype
2022 DALLA BARBA, Francesco; Soardi, Michela; Scano, Martina; Benetollo, Alberto; Carotti, Marcello; Caccin, Paola; Risato, Giovanni; Argenton, Francesco; Sandonà, Dorianna